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Not actual patients.

Gene therapy resources

The resources provided below are designed to broaden your understanding of gene therapy. They were chosen because they provide historical perspective, terms often used, and opportunities for you to discover where and how researchers are studying different potential approaches to treat genetic diseases.


History of gene therapy

How long have scientists explored gene therapy as a way to treat genetic illness? Take a look at this timeline of the remarkable progress made thus far.


Genetic terms

This glossary consists of common terms that refer to genetic diseases and treatment.


Helpful links

Interested in learning where and how researchers are studying the potential of gene therapy for genetic diseases? These helpful resources provide current information on clinical trials and more.


Download PDFs

Printable, portable, and shareable summary of important information around gene therapy.