It looks like you are using an older version of Internet Explorer which is not supported. We advise that you update your browser to the latest version of Microsoft Edge, or consider using other browsers such as Chrome, Firefox or Safari.

Not actual patients.

What is gene therapy?

Gene therapy is changing the way we manage some genetic diseases by targeting missing, nonworking, or faulty genes.

double-helix

What is gene replacement therapy?

Gene replacement is a type of gene therapy that replaces the function of a missing or nonworking gene with a new, working copy of the malfunctioning gene to treat some genetic conditions.

What research is being done in genetic diseases?

Genetic disease research is making important advancements in our understanding of many genetic diseases and how they can be treated.

laboratory-1